Media Library

Understanding spinal muscular atrophy, a rare, neuromuscular genetic disease.

Modified viruses – including adeno-associated viruses – are an efficient way to transport therapeutic genetic material to affected cells.

Early signs of spinal muscular atrophy can be subtle, and often go unseen by clinicians – which is why newborn screening is critical to help obtain a prompt diagnosis.

Manufacturing of gene therapy is complex. Novartis has developed a reproducible manufacturing process.

Novartis Gene Therapies is the world leader in gene therapy, and is reimagining medicine to transform the lives of patients.

A new, state-of-the-art gene therapy manufacturing facility in North Carolina, USA

Gene therapy – an innovative approach to treating rare, genetic diseases.

Chief Strategy & Growth Officer since July 18, 2022

Crizanlizumab clinical setting from international managed access program (MAP) infographic

President, Development and Chief Medical Officer since May 16, 2022

President, US, since April 4, 2022 | Member of the Executive Committee as of May 1, 2022

Content area «Fragility of Life» of the Wonders of Medicine exhibition in the Novartis Pavillon.